Abstract: Hemophilia is a bleeding disorder caused by a deficiency in coagulation factors VIII or IX. Great advances in hemophilia treatment have been achieved in recent decades, with a range of products for prophylaxis now available, the ability to individualize therapy, and resultant improvements in life expectancy and quality of life. Despite these advances, there remains an unresolved burden, both from the disease and its treatment. Real-world data provide an opportunity to understand the experiences of people with hemophilia and gain insight into the areas of greatest unmet need.
